DNA Repair-Deficiency Disorders - 25 Studies Found
Active, not recruiting |
: Autologous Transplant of EFS-ADA Modified Bone Marrow Cells for ADA-Deficient Severe Combined Immunodeficiency (SCID) : ADA-SCID : 2013-05-07 : Genetic: EFS-ADA transduced CD34+ cells from the bone marrow Eligible subjects will undergo bone marrow |
Terminated |
: Hematopoietic Stem Cell Transplantation (HSCT) for Children With SCID Utilizing Alemtuzumab, Plerixafor & Filgrastim : Severe Combined Immunodeficiency : 2010-08-09 :
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Terminated |
: rAd-p53 Gene Therapy for Advanced Oral and Maxillofacial Malignant Tumors : Advanced Oral and Maxillofacial Malignant Tumors : 2009-05-11 :
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Completed |
: MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID : Severe Combined Immunodeficiency : 2008-11-19 : Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr |
Completed |
: Gene Therapy for ADA-SCID : Severe Combined Immunodeficiency Syndrome : 2008-01-08 : Genetic: gene transduced PBL and/or gene transduced HSC infusions of autologous PBL and/or HSC transduce |
Completed |
: Transplantation of Hematopoietic Cells in Children With Severe Combined Immunodeficiency Syndrome : Severe Combined Immunodeficiency : 2005-09-07 :
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Recruiting |
: Genetic Basis of Immunodeficiency : Severe Combined Immunodeficiency : 2003-02-20 |
Completed |
: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency : Severe Combined Immunodeficiency Syndrome : 2001-06-27 : Drug: CD34+ cells transduced with ADA retrovir |
Completed |
: Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency: A Natural History Study : Severe Combined Immunodeficiency : 1999-11-03 :
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Completed |
: Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia : Fanconi Anemia : 2009-08-24 : Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept. |